Molecular and Cell Biology of Human Gene Therapeutics

No abstract is available for this paper.

• Publication year

  1995

• Venue

  Molecular and cell biology of human diseases series

• Publication date

  Unknown publication date

• Fields of study

  Biology, Medicine

• Identifiers
  DOI 10.1007/978-94-011-0547-7
• External record

  Open on Semantic Scholar

• Source metadata

  Semantic Scholar

• No claims are published for this paper.

• No concepts are published for this paper.

• Fusigenic liposome-mediated DNA transfer into cardiac myocytes.

  1996cited by this paper
• [Human gene therapy].

  1996cited by this paper
• MASSIVE COVERT INFECTION OF HELPER T LYMPHOCYTES AND MACROPHAGES BY HIV DURING THE INCUBATION PERIOD OF AIDS

  1995cited by this paper
• Gene therapy for cystic fibrosis.

  1995cited by this paper
• Expression of utrophin (dystrophin‐related protein) and dystrophin‐associated glycoproteins in muscles from patients with Duchenne muscular dystrophy

  1994cited by this paper
• Progress towards gene therapy for HIV infection.

  1994cited by this paper
• Cell and Gene Therapy in Duchenne Muscular Dystrophy

  1994cited by this paper
• Deletion analysis of the dystrophin‐actin binding domain

  1994cited by this paper
• Long-term biological response of injured rat carotid artery seeded with smooth muscle cells expressing retrovirally introduced human genes.

  1994cited by this paper
• Inhibition of vascular smooth muscle cell proliferation in vitro and in vivo by c-myc antisense oligodeoxynucleotides.

  1994cited by this paper
• Gene Transfer in Mammalian Cells Using Liposomes as Carriers

  1994cited by this paper
• Molecular organization at the glycoprotein-complex-binding site of dystrophin. Three dystrophin-associated proteins bind directly to the carboxy-terminal portion of dystrophin.

  1994cited by this paper
• Gene therapy for vascular smooth muscle cell proliferation after arterial injury.

  1994cited by this paper
• Intracellular immunization of human T cells with a hairpin ribozyme against human immunodeficiency virus type 1.

  1994cited by this paper
• Talin, vinculin and DRP (utrophin) concentrations are increased at mdx myotendinous junctions following onset of necrosis.

  1994cited by this paper
• Independent localization of dystrophin N- and C-terminal regions to the sarcolemma of mdx mouse myofibres in vivo.

  1994cited by this paper
• Formation of nascent intercalated disks between grafted fetal cardiomyocytes and host myocardium.

  1994cited by this paper
• A Molecular Genetic Intervention for AIDS—Effects of a Transdominant Negative Form of Rev. Hughes Medical Institute Research Laboratories, Ann Arbor, Michigan

  1994cited by this paper
• Deficiency of merosin in dystrophic dy mice and genetic linkage of laminin M chain gene to dy locus.

  1994cited by this paper
• Does utrophin expression in muscles of mdx mice during postnatal development functionally compensate for dystrophin deficiency?

  1994cited by this paper
• Liposome-mediated gene transfer into human vascular smooth muscle cells.

  1994cited by this paper
• Multiple regions of the human cardiac actin gene are necessary for maturation-based expression in striated muscle.

  1994cited by this paper
• Retroviral-Mediated Gene Transfer and Duchenne Muscular Dystrophy

  1994cited by this paper
• Constitutive Expression of Chimeric Neo-Rev Response Element Transcripts Suppresses HIV-1 Replication in Human CD4+ T Lymphocytes

  1994cited by this paper
• The molecular biology of HIV-1.

  1994cited by this paper
• Retroviral vectors.

  1994influential reference
• Dystroglycan-α, a dystrophin-associated glycoprotein, is a functional agrin receptor

  1994cited by this paper
• Heterogeneity of the 59-kDa dystrophin-associated protein revealed by cDNA cloning and expression.

  1994cited by this paper
• Defective muscle basement membrane and lack of M-laminin in the dystrophic dy/dy mouse.

  1994cited by this paper
• Increased gene expression after liposome-mediated arterial gene transfer associated with intimal smooth muscle cell proliferation. In vitro and in vivo findings in a rabbit model of vascular injury.

  1994cited by this paper
• [Dystrophin-related protein in diaphragm, limb and myoblast transferred muscles of mdx mouse].

  1994cited by this paper
• A role for dystrophin-associated glycoproteins and utrophin in agrin-induced AChR clustering.

  1994cited by this paper
• The emerging family of dystrophin-related proteins.

  1994cited by this paper
• Efficient catheter-mediated gene transfer into the heart using replication-defective adenovirus.

  1994cited by this paper
• Prospects for treating arthritis by gene therapy.

  1994cited by this paper
• Inactivation of E2a in recombinant adenoviruses improves the prospect for gene therapy in cystic fibrosis

  1994cited by this paper
• Exon structure of the human dystrophin gene.

  1993cited by this paper
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  1993cited by this paper
• Chemokines in Cardiovascular Disease

  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
• Interleukin-1 receptor antagonist.

  1993cited by this paper
• HIV infection is active and progressive in lymphoid tissue during the clinically latent stage of disease

  1993cited by this paper
• Intraarticular expression of biologically active interleukin 1-receptor-antagonist protein by ex vivo gene transfer.

  1993cited by this paper
• Systemic gene expression after intravenous DNA delivery into adult mice.

  1993cited by this paper
• Efficient adenovirus-mediated transfer of a human minidystrophin gene to skeletal muscle of mdx mice

  1993cited by this paper
• Systemic immunological effects of cytokine genes injected into skeletal muscle.

  1993cited by this paper
• Augmentation of human immunodeficiency virus type 1 neutralizing antibody by priming with gp160 recombinant vaccinia and boosting with rgp160 in vaccinia-naive adults. The NIAID AIDS Vaccine Clinical Trials Network.

  1993cited by this paper
• Differentiation and long-term survival of C2C12 myoblast grafts in heart.

  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
• Gene therapy for duchenne dystrophy

  1993cited by this paper
• Dystrophin and the membrane skeleton.

  1993cited by this paper
• Adenoviral-mediated gene transfer to rabbit synovium in vivo.

  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
• Embryonic stem cell model systems for vascular morphogenesis and cardiac disorders.

  1993cited by this paper
• Human dystrophin gene transfer: genetic correction of dystrophin deficiency.

  1993cited by this paper
• Transdominant inhibition of wild-type human immunodeficiency virus type 2 replication by an envelope deletion mutant

  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
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  1993cited by this paper
• Heart-specific targeting of firefly luciferase by the myosin light chain-2 promoter and developmental regulation in transgenic mice.

  1993cited by this paper
• Heterologous protection against influenza by injection of DNA encoding a viral protein.

  1993cited by this paper
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  1993cited by this paper
• A nuclear localization signal within HIV-1 matrix protein that governs infection of non-dividing cells

  1993cited by this paper
• Targeting gene expression to specific cardiovascular cell types in transgenic mice.

  1993cited by this paper
• T cell homeostasis in HIV infection: part of the solution, or part of the problem?

  1993cited by this paper
• Dystrophin at the plasma membrane of human muscle fibers shows a costameric localization.

  1992cited by this paper
• Low Level In Vivo Gene Transfer Into the Arterial Wall Through a Perforated Balloon Catheter

  1992cited by this paper
• Antisense c-myb oligonucleotides inhibit intimal arterial smooth muscle cell accumulation in vivo

  1992cited by this paper
• Expression of naked plasmids by cultured myotubes and entry of plasmids into T tubules and caveolae of mammalian skeletal muscle.

  1992cited by this paper
• Human dystrophin expression corrects the myopathic phenotype in transgenic mdx mice.

  1992cited by this paper
• Cellular Engineering for the Treatment of Metabolic Disorders: Prospects for Therapy in Diabetes

  1992cited by this paper
• Deficiency of the 50K dystrophin-associated glycoprotein in severe childhood autosomal recessive muscular dystrophy

  1992cited by this paper
• Long-term expression of human adenosine deaminase in rhesus monkeys transplanted with retrovirus-infected bone-marrow cells.

  1992cited by this paper
• Molecular shape of dystrophin.

  1992cited by this paper

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  2022cites this paper
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  2021cites this paper
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  2018cites this paper
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  2014cites this paper
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  2008cites this paper
• Nanotechnology for Gene Therapy – HVJ‐E Vector

  2007cites this paper
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  2003cites this paper
• Nonneurotropic adenovirus: a vector for gene transfer to the brain and gene therapy of neurological disorders.

  2003cites this paper
• Nonneurotropic adenovirus: a vector for gene transfer to the brain and gene therapy of neurological disorders.

  2003influential citation
• Mouse antibody response to a microsporidian parasite following inoculation with a gene coding for parasite ribosomal RNA.

  2002cites this paper
• Engineering an improved adenovirus packaging cell line

  2002cites this paper
• Indoleamine 2,3-dioxygenase expression in transplanted NOD Islets prolongs graft survival after adoptive transfer of diabetogenic splenocytes.

  2002cites this paper
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  2002cites this paper
• EBV replicon vector system enhances transgene expression in vivo: applications to cancer gene therapy

  2001cites this paper
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  2000cites this paper
• Amplification of transgene expression in vitro and in vivo using a novel inhibitor of histone deacetylase.

  2000cites this paper
• DNA fusion vaccines against B-cell tumors.

  2000cites this paper
• Biotechnology in animal nutrition, physiology and health

  1999cites this paper
• DNA is as effective as protein at inducing antibody in fish.

  1999cites this paper
• Manipulation of pathogen-derived genes to influence antigen presentation via DNA vaccines.

  1999cites this paper
• Progress on Nucleic Acid-Based Vaccines for the Control of Human and Animal Diseases

  1999cites this paper
• DNA vaccines with single-chain Fv fused to fragment C of tetanus toxin induce protective immunity against lymphoma and myeloma

  1998cites this paper
• Co-packaging of sense and antisense RNAs: a novel strategy for blocking HIV-1 replication

  1998cites this paper
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  1997cites this paper
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  1997cites this paper
• Nucleic acid vaccination of sheep: Use in combination with a conventional adjuvanted vaccine against Taenia ovis

  1997cites this paper
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  1997cites this paper
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  1997cites this paper
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  1996cites this paper
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  1996cites this paper
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  1995cites this paper
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  1995cites this paper