Arylsulfatase B activities and glycosaminoglycan levels in retrovirally transduced mucopolysaccharidosis type VI cells. Prospects for gene therapy.

No abstract is available for this paper.

• Publication year

  1996

• Venue

  Journal of Clinical Investigation

• Publication date

  1996-07-15

• Fields of study

  Biology, Medicine

• Identifiers
  DOI 10.1172/JCI118817PMID 8755662PMCID PMC507455
• External record

  Open on Semantic Scholar

• Source metadata

  Semantic Scholar, PubMed

• No claims are published for this paper.

• No concepts are published for this paper.

• Determination of viability of cryopreserved cartilage grafts

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  1994cited by this paper
• Overexpression of N-acetylgalactosamine-4-sulphatase induces a multiple sulphatase deficiency in mucopolysaccharidosis-type-VI fibroblasts.

  1993influential reference
• Arylsulfatase B-deficient mucopolysaccharidosis in rats.

  1993cited by this paper
• Treatment of murine mucopolysaccharidosis type VII by syngeneic bone marrow transplantation in neonates.

  1993cited by this paper
• Structure of the human arylsulfatase B gene.

  1993cited by this paper
• Retroviral-mediated transfer of the human acid sphingomyelinase cDNA: correction of the metabolic defect in cultured Niemann-Pick disease cells.

  1992cited by this paper
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  1992cited by this paper
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  1992cited by this paper
• Correction of human mucopolysaccharidosis type-VI fibroblasts with recombinant N-acetylgalactosamine-4-sulphatase.

  1992cited by this paper
• Restoration of arylsulphatase B activity in human mucopolysaccharidosis-type-VI fibroblasts by retroviral-vector-mediated gene transfer.

  1991cited by this paper
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  1990cited by this paper
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  1983cited by this paper
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  1977cited by this paper
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  1999cites this paper
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  1999cites this paper
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  1999cites this paper
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  1998cites this paper
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