RNA toxicity in human disease and animal models: from the uncovering of a new mechanism to the development of promising therapies.

No abstract is available for this paper.

• Publication year

  2013

• Venue

  Biochimica et Biophysica Acta

• Publication date

  2013-09-01

• Fields of study

  Biology, Medicine

• Identifiers
  DOI 10.1016/j.bbadis.2013.03.002PMID 23500957
• External record

  Open on Semantic Scholar

• Source metadata

  Semantic Scholar, PubMed

• No claims are published for this paper.

• No concepts are published for this paper.

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• CAG repeat RNA as an auxiliary toxic agent in polyglutamine disorders

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• Expanded CUG Repeats Dysregulate RNA Splicing by Altering the Stoichiometry of the Muscleblind 1 Complex*

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• Myotonic dystrophy mouse models: towards rational therapy development.

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• A hexanucleotide repeat expansion in C9ORF72 is the cause of chromosome 9p21-linked ALS-FTD.

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• Triplet Repeat–Derived siRNAs Enhance RNA–Mediated Toxicity in a Drosophila Model for Myotonic Dystrophy

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• Zebrafish deficient for Muscleblind-like 2 exhibit features of myotonic dystrophy

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• Long Tract of Untranslated CAG Repeats Is Deleterious in Transgenic Mice

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