In utero transplantation of fetal liver cells in the mucopolysaccharidosis type VII mouse results in low-level chimerism, but overexpression of beta-glucuronidase can delay onset of clinical signs.

No abstract is available for this paper.

• Publication year

  2001

• Venue

  Blood

• Publication date

  2001-03-15

• Fields of study

  Biology, Medicine

• Identifiers
  DOI 10.1182/BLOOD.V97.6.1625PMID 11238101
• External record

  Open on Semantic Scholar

• Source metadata

  Semantic Scholar, PubMed

• No claims are published for this paper.

• No concepts are published for this paper.

• In utero transplantation of haemopoietic stem cells.

  2001cited by this paper
• Gene Transfer of Low Levels of β-Glucuronidase Corrects Hepatic Lysosomal Storage in a Large Animal Model of Mucopolysaccharidosis VII

  2000cited by this paper
• Gene transfer of low levels of beta-glucuronidase corrects hepatic lysosomal storage in a large animal model of mucopolysaccharidosis VII.

  2000cited by this paper
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  2000cited by this paper
• Molecular basis of feline beta-glucuronidase deficiency: an animal model of mucopolysaccharidosis VII.

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  1999cited by this paper
• A human-murine chimera model for in utero human hematopoietic stem cell transplantation.

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• A kinetic model for the homing and migration of prenatally transplanted marrow.

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  1998cited by this paper
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  1997cited by this paper
• In-utero transplantation of fetal hematopoietic cells in the mouse: the effect of donor and recipient gestational maturity.

  1997cited by this paper
• Murine mucopolysaccharidosis type VII: long term therapeutic effects of enzyme replacement and enzyme replacement followed by bone marrow transplantation.

  1997cited by this paper
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  1994cited by this paper
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• Transplantation of fetal cells.

  1991cited by this paper
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  1990cited by this paper
• A murine model of mucopolysaccharidosis VII. Gross and microscopic findings in beta-glucuronidase-deficient mice.

  1990cited by this paper
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  1990cited by this paper
• Correction of murine mucopolysaccharidosis VII by a human beta-glucuronidase transgene.

  1990cited by this paper
• In-utero transplantation of fetal liver haemopoietic stem cells in monkeys.

  1989cited by this paper
• Induction of hemopoietic chimerism in the caprine fetus by intraperitoneal injection of fetal liver cells

  1989cited by this paper
• Murine mucopolysaccharidosis type VII. Characterization of a mouse with beta-glucuronidase deficiency.

  1989cited by this paper
• Mammalian beta-glucuronidase: genetics, molecular biology, and cell biology.

  1989cited by this paper
• The Metabolic basis of inherited disease

  1989cited by this paper
• The complete nucleotide sequence of murine beta-glucuronidase mRNA and its deduced polypeptide.

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• β-Glucuronidase Deficiency in a Dog: a Model of Human Mucopolysaccharidosis VII

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• Prevention of genetic anemias in mice by microinjection of normal hematopoietic stem cells into the fetal placenta.

  1979cited by this paper
• Beta glucuronidase deficiency: report of clinical, radiologic, and biochemical features of a new mucopolysaccharidosis.

  1973cited by this paper
• TREATMENT OF ENURESIS.

  1964cited by this paper
• The metabolic basis of inherited disease

  1961cited by this paper

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