Long-Term Efficacy of Adeno-Associated Virus Serotypes 8 and 9 in Hemophilia A Dogs and Mice

No abstract is available for this paper.

• Publication year

  2006

• Venue

  Human Gene Therapy

• Publication date

  2006-04-01

• Fields of study

  Medicine

• Identifiers
  DOI 10.1089/hum.2006.17.427PMID 16610930
• External record

  Open on Semantic Scholar

• Source metadata

  Semantic Scholar, PubMed

• No claims are published for this paper.

• No concepts are published for this paper.

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• A Review of the Rationale for Gene Therapy for Hemophilia A With Inhibitors: One-Shot Tolerance and Treatment?

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• Chimeric Mice Engrafted With Canine Hepatocytes Exhibits Similar AAV Transduction Efficiency to Hemophilia B Dog

  2022cites this paper
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• Hemophilia therapy: the future has begun

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• A long-term study of AAV gene therapy in hemophilia A dogs identifies clonal expansions of transduced liver cells

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• Translational Potential of Immune Tolerance Induction by AAV Liver-Directed Factor VIII Gene Therapy for Hemophilia A

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• Protein-Engineered Coagulation Factors for Hemophilia Gene Therapy

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• Evaluation of the activity levels of rat FVIII and human FVIII delivered by adeno-associated viral vectors both in vitro and in vivo.

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